Sep. 25, 2024 — Adults with hemophilia B saw their number of bleeding episodes drop by an average of 71 percent after a single infusion of gene therapy, according to the new results of an ...

These results pave the way for more effective gene therapies for neuromuscular diseases, while reducing the risk of side-effects and production costs. The article, published in Nature ...

Vironexis Biotherapeutics has unveiled with $26 million and a clinical-trial-ready gene therapy that has already nabbed FDA fast track and rare pediatric disease tags. The San Diego-based biotech ...

Gene Park is a reporter for The Washington Post, covering video games and gaming culture. He joined The Post in 2015 as audience editor, and is a former reporter in the West Coast and Pacific region.

Oct. 8, 2024 — A research team describes how they engineered an efficient new enzyme that can produce a synthetic genetic material called threose nucleic acid. The ability to synthesize ...

What Causes JAK2 Gene Mutations? The most common JAK2 mutation found in blood disorders is known as JAK2 V617F, named for a mutation at a specific location in the JAK2 gene. Rather than being ...